Evaluating the safety and effects of VX-407 in healthy individuals

A Phase 1, Randomized, Double-blind, Placebo-controlled, First-in-human Study Evaluating the Safety, Tolerability, and Pharmacokinetics of Single and Multiple Ascending Doses of VX-407 in Healthy Subjects

PHASE1 · Vertex Pharmaceuticals Incorporated · NCT06345755

This study is testing a new drug called VX-407 in healthy people to see if it's safe and how it works in the body, which could help in treating conditions like Autosomal Dominant Polycystic Kidney Disease.

Quick facts

PhasePHASE1
Study typeInterventional
Enrollment119 (estimated)
Ages18 Years to 55 Years
SexAll
SponsorVertex Pharmaceuticals Incorporated (industry)
Locations2 sites (Lenexa, Kansas and 1 other locations)
Trial IDNCT06345755 on ClinicalTrials.gov

What this trial studies

This clinical trial aims to assess the safety, tolerability, and pharmacokinetics of a drug called VX-407 in healthy participants. The study will involve administering VX-407 and a placebo to evaluate how the drug is processed in the body and its overall safety profile. Participants will be monitored for any adverse effects and how their bodies respond to the medication. The findings from this trial could provide important insights into the drug's potential use for treating conditions like Autosomal Dominant Polycystic Kidney Disease (ADPKD).

Who should consider this trial

Good fit: Ideal candidates for this study are healthy adults with a BMI between 18.0 and 32.0 kg/m² and a body weight greater than 50 kg.

Not a fit: Patients with a history of acute illnesses or conditions affecting drug absorption may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could lead to a new treatment option for patients with ADPKD.

How similar studies have performed: Other studies evaluating similar pharmacological approaches have shown promise, but this specific drug's effects are novel.

Eligibility criteria

Show full inclusion / exclusion criteria
Key Inclusion Criteria:

* Body mass index (BMI) of 18.0 to 32.0 kilogram per meter square (kg/m\^2)
* A total body weight of greater than (\>) 50 kg
* Nonsmoker or ex-smoker for at least 3 months before screening

Key Exclusion Criteria:

* History of febrile illness or other acute illness that has not fully resolved within 14 days before the first dose of study drug
* Any condition possibly affecting drug absorption

Other protocol defined Inclusion/Exclusion criteria may apply.

Where this trial is running

Lenexa, Kansas and 1 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Autosomal Dominant Polycystic Kidney Disease

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.