Effect of a diabetes drug on kidney stone formation in cystinuria patients

The Effect of Sodium-glucose Cotransporter (SGLT) 2 Inhibitors on Cystine Stone Formation: A Preliminary Study

Phase 2 Interventional University of California, San Francisco · NCT04818034

This study is testing if a diabetes drug can help people with cystinuria reduce the formation of kidney stones.

Quick facts

PhasePhase 2
Study typeInterventional
Enrollment10 (estimated)
Ages18 Years and up
SexAll
SponsorUniversity of California, San Francisco Academic / other
Locations1 site (San Francisco, California)
Trial IDNCT04818034 on ClinicalTrials.gov

What this trial studies

This study investigates the impact of dapagliflozin, an SGLT-2 inhibitor, on cystine stone formation in patients diagnosed with cystinuria. It is a single-center, proof of concept trial involving five participants who will receive daily oral doses of the medication for up to four weeks. The primary goal is to assess changes in cystine levels in freshly voided urine, with a total study duration of six months. Participants must have a history of cystine kidney stones and are not currently on any other treatments for their condition.

Who should consider this trial

Good fit: Ideal candidates are adults aged 18 or older with a documented history of cystinuria and previous cystine kidney stones.

Not a fit: Patients with a prior diagnosis of diabetes mellitus or those currently taking SGLT-2 inhibitors will not benefit from this study.

Why it matters

Potential benefit: If successful, this approach could provide a new treatment option for patients suffering from recurrent cystine kidney stones.

How similar studies have performed: While the use of SGLT-2 inhibitors for cystinuria is a novel approach, similar studies have shown promise in other conditions, indicating potential for success.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* males and females age 18 or older
* documented cystinuria on prior 24-hour urine collection and/or stone analysis
* history of previous cystine kidney stones
* able and willing to provide consent

Exclusion Criteria:

* prior diagnosis of diabetes mellitus (type I or type II)
* current SGLT-2 inhibitor administration at the time of screening
* SGLT-2 inhibitor administration within the last year prior to screening
* vulnerable populations including incarceration status
* anticipation of pregnancy during the study duration
* unable to give informed consent
* non-English primary language
* pregnancy, lactation, or child- bearing age without birth control devices
* serious illness likely to cause death within the next 5 years.

Where this trial is running

San Francisco, California

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Cystinuria
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.