Comparing conditioning regimens for patients with acute myeloid leukemia or myelodysplastic syndromes

Multiple-center Randomized Study to Compare Fludarabine and Busulfan Versus Fludarabine, Busulfan and Melphalan in Adult Patients With Acute Myeloid Leukemia (AML) and Myelodysplasia Syndrome (MDS)

Phase 3 Interventional Shanghai Jiao Tong University School of Medicine · NCT05991908

This study is testing two different treatment plans for adults with acute myeloid leukemia or myelodysplastic syndromes to see which one helps prevent the disease from coming back after a stem cell transplant.

Quick facts

PhasePhase 3
Study typeInterventional
Enrollment222 (estimated)
Ages16 Years to 55 Years
SexAll
SponsorShanghai Jiao Tong University School of Medicine Academic / other
Drugs / interventionsFludarabine
Locations9 sites (Fuzhou, Fujian and 8 other locations)
Trial IDNCT05991908 on ClinicalTrials.gov

What this trial studies

This study aims to compare the outcomes of two different conditioning regimens for adult patients with acute myeloid leukemia (AML) or myelodysplastic syndromes (MDS) undergoing allogeneic stem cell transplantation (allo-HSCT). One regimen consists of fludarabine and busulfan, while the other includes fludarabine, busulfan, and melphalan. The goal is to determine which regimen results in a lower incidence of disease relapse post-transplantation. The study is conducted across multiple centers and involves random assignment of participants to each treatment group.

Who should consider this trial

Good fit: Ideal candidates include adults with AML in first complete remission or MDS with specific bone marrow blast percentages, who have suitable HLA-matched donors.

Not a fit: Patients with active infections, certain organ dysfunctions, or those with specific viral infections like HIV may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could lead to improved transplantation outcomes and lower relapse rates for patients with AML and MDS.

How similar studies have performed: Previous studies have shown promising results with dual alkylating agent regimens, suggesting potential for success in this approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* acute myeloid leukemia (acute promyelocytic leukemia excluded) in 1st complete remission
* myelodysplasia syndrome with bone marrow blast \>5% and remaining less than 20% at transplantation
* patients with HLA matched sibling donor, 9-10 matched unrelated donor or haplo-identical related donors
* inform consent provided

Exclusion Criteria:

* AML patients with active CNS or extramedullary diseases
* patients with active viral, bacterial or fungal infection
* patients with hepatitis B virus \>1X103 copy/ml
* patients with abnormal liver function, renal function, respiratory or cardiac dysfunction
* patients with uncontrolled mental disorders
* patients with HIV

Where this trial is running

Fuzhou, Fujian and 8 other locations

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Acute Myeloid LeukemiaMyelodysplastic Syndromesconditioning regimen, melphalan, busulfan, fludarabine
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.