Combining Hetrombopag with Dexamethasone for Treating Newly Diagnosed Immune Thrombocytopenia

High-dose Dexamethasone Plus Hetrombopag Versus High-dose Dexamethasone Alone as Frontline Treatment for Newly Diagnosed Adult Primary Immune Thrombocytopenia (ITP):A Prospective Multicenter Randomized Trial

Phase 2 Interventional Shandong University · NCT05943691

This study is testing if combining hetrombopag with high-dose dexamethasone can help adults who are newly diagnosed with immune thrombocytopenia have better platelet counts and fewer bleeding symptoms.

Quick facts

PhasePhase 2
Study typeInterventional
Enrollment100 (estimated)
Ages18 Years and up
SexAll
SponsorShandong University Academic / other
Drugs / interventionsPrednisone
Locations1 site (Dongying, Shandong)
Trial IDNCT05943691 on ClinicalTrials.gov

What this trial studies

This clinical trial investigates the efficacy and safety of hetrombopag combined with high-dose dexamethasone in adults newly diagnosed with primary immune thrombocytopenia (ITP). A total of 100 participants will be randomly assigned to receive either the combination treatment or high-dose dexamethasone alone. The treatment involves administering hetrombopag at a starting dose of 5 mg daily for 8 weeks, with adjustments based on platelet counts, alongside a 4-day course of dexamethasone. The study aims to evaluate platelet counts, bleeding symptoms, and adverse events throughout the treatment period.

Who should consider this trial

Good fit: Ideal candidates for this study are adults over 18 years old with newly diagnosed immune thrombocytopenia and specific platelet count criteria.

Not a fit: Patients with secondary thrombocytopenia, recent thromboembolism, or significant liver or kidney dysfunction may not benefit from this study.

Why it matters

Potential benefit: If successful, this treatment could provide a more effective option for managing newly diagnosed ITP, potentially improving patient outcomes.

How similar studies have performed: While this approach is novel in combining hetrombopag with high-dose dexamethasone, similar studies have shown promise in treating ITP with other therapies.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Older than 18 years
* Meet the diagnostic criteria for newly diagnosed immune thrombocytopenia (diagnosed within 3 month);
* platelet count \<30\*10\^9/L, or \< 50\*10\^9/L with bleeding manifestations, both;
* Willing and able to sign written informed consent

Exclusion Criteria:

* secondary thrombocytopenia or graded MF≥2 myelofbrosis based on the European Consensus Scale
* Previous history of treatment for ITP, except Platelet transfusion, ITP-directed Prednisone therapy no more than 2 weeks or TPO therapy no more than 1 week and stopped ≥1 week before randomization
* No response to TPO-RA or rhTPO
* HIV, hepatitis C or B virus infection
* pregnancy or lactation;
* arterial or venous thromboembolism within the 6 months before screening
* total bilirubinalanine, aminotransferase or aspartate transaminase\>3×upper limit of normal (ULN), serum creatinine\>1.5×ULN
* congestive heart failure (New York Heart Association \[NYHA\] class III/IV);
* neoplastic disease within the past 5 years;
* liver cirrhosis
* people who could not adhere to the protocol or were planning to have a surgical procedure in 6 months.

Where this trial is running

Dongying, Shandong

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions ITP - Immune ThrombocytopeniaHetrombopag, Dexamethasone
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.