Combined therapy of low-dose ATRA and attenuated ATO for promyelocytic leukemia

Effectiveness and Safety of Therapy Based on Attenuated Arsenic Trioxide Plus Low Doses of All-trans Retinoic Acid as Remission Induction Therapy in Patients With Acute Promyelocytic Leukemia Phase 1/2 Clinical Trial

Phase1; Phase2 Interventional Hospital Universitario Dr. Jose E. Gonzalez · NCT05497310

This study is testing a new treatment using low doses of two medications for adults with acute promyelocytic leukemia to see if it can help them without causing too many side effects.

Quick facts

PhasePhase1; Phase2
Study typeInterventional
Enrollment15 (estimated)
Ages18 Years and up
SexAll
SponsorHospital Universitario Dr. Jose E. Gonzalez Academic / other
Locations1 site (Monterrey, Nuevo Leon)
Trial IDNCT05497310 on ClinicalTrials.gov

What this trial studies

This clinical trial aims to evaluate the effectiveness and safety of a combined therapy using low-dose all-trans retinoic acid (ATRA) and attenuated arsenic trioxide (ATO) in patients with acute promyelocytic leukemia (APL). The study will include adults with newly diagnosed or relapsed APL who have not previously received ATO treatment. By utilizing lower doses of ATRA and ATO, the trial seeks to maintain therapeutic efficacy while reducing associated toxicities. The trial is designed as a phase 1/2, non-randomized, single-center study to assess the outcomes of this treatment regimen.

Who should consider this trial

Good fit: Ideal candidates for this study are adults over 18 years old with a new diagnosis of APL or relapsed APL who have not been previously treated with ATO.

Not a fit: Patients with poor functional status, significant organ dysfunction, or recent cardiovascular issues may not benefit from this study.

Why it matters

Potential benefit: If successful, this therapy could provide a safer and effective treatment option for patients with APL, particularly those with limited resources.

How similar studies have performed: Other studies have shown promising results with similar low-dose regimens in APL, indicating potential for success in this approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Age \>18 years
* Both genders
* new diagnosis of APL
* Diagnosis of relapsed APL who have not been previously treated with ATO
* Morphological diagnosis of APL confirmed by PCR or FISH

Exclusion Criteria:

* Poor functional status (ECOG\>2)
* Organic dysfunction (Marshall score ≥2)
* Pregnancy
* Heart failure (NYHA III or IV)
* Renal failure (GFR \<30 ml/min/1.72m2)
* History of ventricular arrhythmias or uncontrolled arrhythmias
* Acute myocardial infarction, unstable angina, or stable angina in the last six months
* Uncontrolled active infection
* Liver disease (Child-Pugh C)

Where this trial is running

Monterrey, Nuevo Leon

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.
Conditions Promyelocytic Leukemiaall-trans retinoic acidarsenic trioxidefrontline therapyinduction chemotherapy
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.