Access to Ivosidenib for Patients with Advanced Cholangiocarcinoma

An Open-Label Early Access Phase 3b Study of Ivosidenib in Patients With a Pretreated Locally Advanced or Metastatic Cholangiocarcinoma

PHASE3 · Servier · NCT05876754

This study is testing if a daily pill called ivosidenib can help adults with advanced bile duct cancer feel better and live longer after their previous treatments.

Quick facts

PhasePHASE3
Study typeInterventional
Enrollment220 (estimated)
Ages18 Years and up
SexAll
SponsorServier (industry)
Drugs / interventionsradiation
Locations84 sites (Yerevan and 83 other locations)
Trial IDNCT05876754 on ClinicalTrials.gov

What this trial studies

This Phase 3b study evaluates the safety and effectiveness of ivosidenib in adult patients with previously treated, locally advanced, or metastatic cholangiocarcinoma. Participants will take 500 mg of ivosidenib orally once daily for 28-day cycles, with treatment continuing as long as clinical benefit is observed. The study includes a minimum of six visits over 18 months to monitor health outcomes and quality of life. It aims to gather additional data on the drug's impact in this patient population.

Who should consider this trial

Good fit: Ideal candidates are adults with nonresectable or metastatic cholangiocarcinoma who have specific gene mutations and have previously undergone systemic therapy.

Not a fit: Patients who have received prior IDH1 inhibitors or those with recent systemic cancer treatment may not benefit from this study.

Why it matters

Potential benefit: If successful, this study could provide a new effective treatment option for patients with advanced cholangiocarcinoma.

How similar studies have performed: Other studies have shown positive outcomes with similar treatments, indicating potential for success in this approach.

Eligibility criteria

Show full inclusion / exclusion criteria
Inclusion Criteria:

* Diagnosis of nonresectable or metastatic Cholangiocarcinoma (CCA), not eligible for curative-intent resection, transplantation, or ablative therapies
* Have a documented IDH1 R132C, R132L, R132G, R132H, or R132S gene-mutated disease
* Have tried at least 1 prior type of systemic therapy for CCA, and have recovered from any side effects
* Female patients of childbearing potential must have a negative blood pregnancy test prior to starting treatment and must agree to use 2 forms of contraception from the time they enroll to 1 month after their last dose of study drug
* Male patients with a female partner with childbearing potential must also agree to use 2 forms of contraception from the time they enroll to 1 month after their last dose of study drug

Exclusion Criteria:

* Received a prior IDH1 inhibitor
* Have received a transplant
* Have received systemic cancer treatment or radiotherapy within 2 weeks prior to Day 1 of Cycle 1
* Have received hepatic radiation, chemoembolization, and radiofrequency ablation within 4 weeks prior to Day 1 of Cycle 1
* Have ongoing brain metastases requiring steroids
* Have underwent major surgery within 4 weeks of Day 1 of Cycle 1 prior to C1D1
* Have an active hepatitis B (HBV) or hepatitis C (HCV) infections, known positive human immunodeficiency virus (HIV) antibody results, or acquired immunodeficiency syndrome (AIDS) related illness
* Are pregnant or breastfeeding

Where this trial is running

Yerevan and 83 other locations

+34 more sites — see ClinicalTrials.gov for the full list.

Study contacts

How to participate

  1. Review the eligibility criteria above with your treating physician.
  2. Visit the official trial page on ClinicalTrials.gov for the most current contact information and recruitment status.
  3. Contact the listed study coordinator or principal investigator to request pre-screening. Pre-screening is free and never obligates you to enroll.

View on ClinicalTrials.gov →

Conditions: Cholangiocarcinoma, CCA, Pretreated locally advanced or metastatic cholangiocarcinoma

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.