Sponsor or institution

Clinical trials and research at Phoenix Nest, INC.

• 6NIH research projects

NIH-funded research (6)

Early-stage science funded by the US National Institutes of Health. Most of these projects don't enroll patients, but they show what is being worked on.

• Gene therapy manufacturing and testing for a rare brain disease (MPS IIIC) to help affected children

  A NIH-funded project aims to develop and refine the manufacturing and analytical processes for a gene therapy intended to help children with MPS IIIC, a rare and progressive neurological disease.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-11315125

• Biomarkers and clinical tools for Sanfilippo syndrome type C (MPS IIIC)

  Create new lab tests and clinical tools to help detect and follow MPS IIIC (Sanfilippo type C) in affected children and adults.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-11128545

• Finding new biomarkers and tools for Mucopolysaccharidosis IIIC patients.

  This study is looking for ways to better diagnose and manage Mucopolysaccharidosis Type IIIC, a rare condition, by finding helpful markers in the body and improving how we track the disease, so patients can get better care and support.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-10921133

• Investigating treatments for a rare childhood brain disorder called MPS IIID.

  This study is looking at a new treatment for Mucopolysaccharidosis IIID, a rare condition that affects how children's brains develop, and it aims to help improve their quality of life by delivering a special enzyme directly into the brain.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-10893861

• Investigating a new treatment for a rare childhood neurodegenerative disorder.

  This study is testing a new treatment that delivers a special enzyme directly into the brain to help children with Mucopolysaccharidosis IIID, a rare condition that affects their development and thinking skills, with the hope of improving their health and quality of life.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-10831385

• Creating a gene therapy for Sanfilippo Syndrome Type C

  This study is testing a new gene therapy for people with Sanfilippo Syndrome Type C, a rare condition that affects the brain, to see if it can help by fixing the genetic problem that causes the disease and improve their quality of life.

  NIH research Phoenix Nest, INC. · Brooklyn, United States · NIH-10706562

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