Sponsor or institution
Clinical trials and research at Myogene Bio, LLC
As of November 12, 2026, Find a Trial lists 5 NIH-funded research projects at this institution, with $2.4 million in listed awards. Every study is explained in plain English. Data from ClinicalTrials.gov and NIH RePORTER, updated November 12, 2026.
- 5NIH research projects
NIH-funded research (5)
Early-stage science funded by the US National Institutes of Health. Most of these projects don't enroll patients, but they show what is being worked on.
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Advancing manufacturing and release testing for a Duchenne gene editing therapy
A project to optimize how a dual-vector AAV gene editing treatment for Duchenne muscular dystrophy is made and tested, so it can move toward clinical use.
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Durable gene edit to restore dystrophin in Duchenne muscular dystrophy
A gene-editing approach aims to restore dystrophin for people with Duchenne muscular dystrophy by removing DMD exons 45–55 to produce a long-lasting fix.
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Restoring a working, internally shortened dystrophin protein for Duchenne muscular dystrophy
This project looks at a gene-editing approach delivered by AAV that creates a shortened but working dystrophin to help people with Duchenne muscular dystrophy.
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Evaluating a gene editing therapy for Duchenne muscular dystrophy
This study is testing a new gene editing treatment for Duchenne muscular dystrophy that aims to fix the gene responsible for the condition, and it's designed to help people with this muscle-wasting disease by improving their muscle function over time.
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Gene editing therapy to restore dystrophin in Duchenne muscular dystrophy
This study is testing a new gene editing treatment for Duchenne muscular dystrophy that uses CRISPR technology to fix the genetic problems causing the disease, and it's being done in mice to see how well it works over a longer time, which could lead to better options for patients in the future.
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