Why immunotherapy works less well for NASH-related liver cancer

Determinants of immunotherapy response in NASH-Hepatocellular carcinoma

NIH-funded research Icahn School of Medicine at Mount Sinai · NIH-11144259

This project tests whether adding drugs that block KIT/MAPK/Wnt pathways to immunotherapy helps people with NASH-related liver cancer respond better.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionIcahn School of Medicine at Mount Sinai NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11144259 on NIH RePORTER

What this research studies

From a patient's perspective, researchers are studying why liver cancer that develops from non-alcoholic steatohepatitis (NASH) often resists immune-based treatments and whether combining immunotherapy with drugs that target KIT/MAPK/Wnt signaling can overcome that resistance. The team will use patient tumor samples, gene signatures, 3D cell cultures, and animal models to study immune cell behavior and identify biomarkers linked to response. They will look for molecular markers in biopsies and blood that predict who might benefit from combination therapies. The goal is to find measurable tests and treatment combinations that could be taken into early clinical testing.

Who could benefit from this research

Good fit: Ideal candidates are people with hepatocellular carcinoma caused by NASH, especially those eligible for systemic immunotherapy and willing to provide biopsy or blood samples.

Not a fit: Patients with liver cancer from non-NASH causes or those unable to receive immunotherapy or pathway-targeting drugs may not benefit from the specific strategies studied here.

Why it matters

Potential benefit: If successful, this work could lead to new combination therapies and biomarkers that help more people with NASH-related hepatocellular carcinoma respond to immunotherapy.

How similar studies have performed: Atezolizumab plus bevacizumab already improves survival in HCC, but adding KIT/MAPK/Wnt blockers for NASH-HCC is a newer, largely experimental approach.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.