Vorasidenib plus PEP-IDH1M vaccine for recurrent IDH1-mutant glioma

Clinical evaluation and non-invasive monitoring of Vorasidenib in combination with tumor specific peptide PEP-IDH1M vaccine therapy in patients with recurrent mutant IDH1 glioma

NIH-funded research Duke University · NIH-11178424

Combining an oral drug called vorasidenib with a vaccine that targets the mutant IDH1 protein aims to help adults with recurrent IDH1-mutant glioma while using MRI-based spectroscopy to watch tumor chemistry.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionDuke University NIH-funded
Lab location1 site (Durham, United States)
Project IDNIH-11178424 on NIH RePORTER

What this research studies

You would take an oral drug called vorasidenib and receive a tumor-specific peptide vaccine (PEP-IDH1M) intended to teach your immune system to recognize the IDH1-mutant tumor. Doctors will use non-invasive magnetic resonance spectroscopy (MRS) alongside standard MRI, blood tests, and clinic visits to track a tumor chemical called 2HG and other signs of response. The hope is that lowering 2HG will reduce immune suppression and let vaccine-primed T cells better attack the tumor. Study visits, imaging, dosing, and safety monitoring would occur at the study site.

Who could benefit from this research

Good fit: Adults with recurrent glioma whose tumor carries the IDH1 mutation and who meet medical and imaging eligibility criteria would be the ideal candidates.

Not a fit: People without an IDH1-mutant tumor or those with rapidly progressive high-grade glioblastoma are unlikely to benefit from this targeted combination.

Why it matters

Potential benefit: If successful, this approach could slow tumor growth, improve symptoms or quality of life, and give doctors a non-invasive way to watch treatment effects.

How similar studies have performed: Vorasidenib and IDH1-targeted peptide vaccines have shown promise separately in early work, but combining them and pairing with MRS monitoring is a more recent and less tested approach.

Where this research is happening

Durham, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.