Using live bacteria to treat homocystinuria

Live microbial therapeutics: an enhanced treatment paradigm for classical homocystinuria

NIH-funded research Petri Bio LLC · NIH-10921820

This study is testing a new treatment using specially designed bacteria to help people with homocystinuria lower their harmful homocysteine levels, making it easier and more comfortable for them to manage their condition without strict diets or side effects.

Quick facts

Grant typeSbir 2 grant
Study typeNIH-funded research
Funding institutionPetri Bio LLC NIH-funded
Lab location1 site (Los Angeles, United States)
Project IDNIH-10921820 on NIH RePORTER

What this research studies

This research focuses on developing a synthetic live bacterial therapy for homocystinuria (HCU), a rare metabolic disorder that causes harmful levels of homocysteine in the body. The approach aims to utilize specific bacteria that can break down methionine in the gut, thereby reducing homocysteine levels in patients. Current treatments often involve strict dietary restrictions and supplements, which can be difficult for patients to adhere to and may cause unpleasant side effects. By using engineered bacteria, this therapy seeks to provide a more effective and tolerable treatment option for individuals with HCU.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with pyridoxine non-responsive homocystinuria, particularly those struggling with current treatment regimens.

Not a fit: Patients with other forms of homocystinuria that respond to pyridoxine or those without a diagnosis of homocystinuria may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could offer a more effective and manageable treatment for patients with homocystinuria, potentially improving their quality of life.

How similar studies have performed: While the use of live microbial therapeutics is a growing field, this specific approach for treating homocystinuria is novel and has not been extensively tested in prior studies.

Where this research is happening

Los Angeles, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.