Understanding the genetics of molybdenum cofactor

Genetic analyses of molybdenum cofactor biology

NIH-funded research Sanford Research/usd · NIH-11132895

This research explores how a vital substance called molybdenum cofactor, or Moco, works in the body to help us understand a rare and serious genetic condition.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionSanford Research/usd NIH-funded
Lab location1 site (Sioux Falls, United States)
Project IDNIH-11132895 on NIH RePORTER

What this research studies

Molybdenum cofactor (Moco) is a crucial component that all animals need to live, helping important enzymes in our bodies function correctly. When there are problems with the genes that make Moco, it leads to a rare and often deadly condition called human Moco deficiency. This condition affects how the body processes sulfur amino acids and purines, which are essential for health. Our goal is to uncover new ways animals maintain Moco balance and identify genetic pathways that control Moco-related metabolism. We use a small worm called C. elegans as a model to discover these fundamental biological processes.

Who could benefit from this research

Good fit: This foundational research is not directly recruiting patients but aims to benefit those affected by or at risk for human Moco deficiency in the future.

Not a fit: Patients without human Moco deficiency or related metabolic disorders would not directly benefit from this specific research.

Why it matters

Potential benefit: If successful, this work could lead to a deeper understanding of Moco deficiency, potentially paving the way for new treatments or therapies for this rare and lethal genetic disorder.

How similar studies have performed: This project builds on recent discoveries about how Moco is transported in animals, suggesting a novel and promising area of investigation.

Where this research is happening

Sioux Falls, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.