Understanding the Effects of ATP1A3 Gene Changes

Clinical, Genetic, and Cellular Consequences of Mutations In NA,K-ATPase ATP1A3

NIH-funded research State University of New York at Buffalo · NIH-11123904

This project aims to better understand how changes in the ATP1A3 gene affect the brain and body in youth and adults.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionState University of New York at Buffalo NIH-funded
Lab location1 site (Amherst, United States)
Project IDNIH-11123904 on NIH RePORTER

What this research studies

Our team is looking closely at the ATP1A3 gene to understand how its changes lead to various symptoms, including problems with movement, thinking, and mental health. We are gathering information from patients to learn more about their experiences and discover new ways the gene might affect them. We also use laboratory tests to confirm how these gene changes cause problems and to explore if existing medications could help. The goal is to create a full picture of how ATP1A3 conditions progress and to find potential treatments for the future.

Who could benefit from this research

Good fit: Ideal candidates are youth and adults aged 21 and older who have conditions linked to mutations in the ATP1A3 gene, including those with motor, cognitive, or psychological symptoms.

Not a fit: Patients with conditions unrelated to the ATP1A3 gene or those primarily experiencing severe infantile manifestations may not directly benefit from this specific focus.

Why it matters

Potential benefit: If successful, this work could lead to a better understanding of ATP1A3-related conditions, helping to develop new treatments and improve the quality of life for affected individuals.

How similar studies have performed: While the specific range of ATP1A3 symptoms in youth and adults is still being mapped, previous research has established the gene's importance, and similar approaches have been used to understand other genetic conditions.

Where this research is happening

Amherst, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.