Understanding how the body's own genetic material can cause brain inflammation

Investigation of Self-Nucleic Acids as a Trigger for Neuroinflammation

NIH-funded research Columbia University Health Sciences · NIH-11093351

This research explores how our body's own genetic material might mistakenly trigger inflammation in the brain, especially in conditions like Aicardi-Goutières syndrome and ALS.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionColumbia University Health Sciences NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11093351 on NIH RePORTER

What this research studies

Our bodies have a natural defense system that usually recognizes harmful invaders like viruses. This project looks into whether this same defense system can sometimes mistakenly identify our own genetic material as a threat, leading to inflammation, particularly in the brain. Researchers are studying how a specific enzyme, ADAR1, helps prevent this confusion and what happens when it doesn't work correctly, as seen in conditions like Aicardi-Goutières syndrome. Understanding this process could help us learn more about the causes of brain inflammation in diseases such as ALS.

Who could benefit from this research

Good fit: This foundational research is for patients with conditions like Aicardi-Goutières syndrome and Amyotrophic Lateral Sclerosis (ALS) who are interested in understanding the underlying causes of their disease.

Not a fit: Patients whose conditions are not related to immune system overactivity or genetic material misidentification may not directly benefit from this specific line of inquiry.

Why it matters

Potential benefit: If successful, this work could lead to new ways to prevent or treat neuroinflammation and autoimmune conditions by targeting how the body's immune system reacts to its own genetic material.

How similar studies have performed: Prior studies on Aicardi-Goutières syndrome have already shown a connection between self-nucleic acid activation and autoimmune responses, providing a foundation for this work.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Aicardi Goutieres syndromeAmyotrophic Lateral Sclerosis Motor Neuron Disease
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.