Understanding how specific gene mutations affect leukemia treatment

Interrogating the minor spliceosome to understand and treat leukemia

['FUNDING_R01'] · SLOAN-KETTERING INST CAN RESEARCH · NIH-10876993

This study is looking at how changes in the ZRSR2 gene affect leukemia, especially in people with myelodysplastic syndromes, to find better ways to treat the disease.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorSLOAN-KETTERING INST CAN RESEARCH (nih funded)
Locations1 site (NEW YORK, UNITED STATES)
Trial IDNIH-10876993 on ClinicalTrials.gov

What this research studies

This research investigates the role of mutations in the ZRSR2 gene, which is associated with leukemia, particularly in patients with myelodysplastic syndromes. The team aims to explore how these mutations impact the function of RNA splicing and how they can be targeted for therapeutic purposes. By analyzing the genetic and functional consequences of these mutations, the research seeks to improve treatment strategies for leukemia patients. Patients may be involved in studies that assess the effects of these mutations on their condition and treatment responses.

Who could benefit from this research

Good fit: Ideal candidates for this research are patients diagnosed with myelodysplastic syndromes or other myeloid malignancies who have mutations in the ZRSR2 gene.

Not a fit: Patients without these specific genetic mutations or those with other types of leukemia may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatments for leukemia by targeting specific genetic mutations.

How similar studies have performed: While the focus on ZRSR2 mutations is relatively novel, similar research on other spliceosomal mutations has shown promising results in understanding and treating leukemia.

Where this research is happening

NEW YORK, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Cancers

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.