Understanding how mutant prion proteins accumulate in brain cells

Mechanisms of Mutant Prion Protein Aggregation Within Endolysosomal Pathways

NIH-funded research Scripps Research Institute, the · NIH-11101284

This study is looking at how certain misfolded proteins build up in brain cells and cause problems, especially in conditions like Alzheimer's disease, to help find new ways to treat these issues and improve care for patients.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionScripps Research Institute, the NIH-funded
Lab location1 site (La Jolla, United States)
Project IDNIH-11101284 on NIH RePORTER

What this research studies

This research investigates the mechanisms behind the accumulation of misfolded prion proteins in brain cells, particularly focusing on their aggregation within endolysosomal pathways. By studying human brain samples affected by prion diseases, the researchers aim to identify the pathways that lead to the formation of neurotoxic aggregates known as endoggresomes. The study employs advanced imaging techniques to analyze the structural changes in neurons and aims to uncover potential targets for pharmacological treatment of Alzheimer's disease and related dementias. Patients may benefit from insights gained into the underlying causes of these conditions, which could lead to new therapeutic strategies.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with Alzheimer's disease or related dementias, particularly those with familial prion mutations.

Not a fit: Patients with non-neurodegenerative conditions or those without any form of dementia may not receive benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments for Alzheimer's disease and related dementias by targeting the mechanisms of protein aggregation.

How similar studies have performed: Previous research has shown promising results in understanding protein aggregation in neurodegenerative diseases, suggesting that this approach may yield valuable insights.

Where this research is happening

La Jolla, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Alzheimer disease dementiaAlzheimer syndrome
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.