Understanding how microglia contribute to ALS and frontotemporal dementia

Microglia contribution to disease pathogenesis in C9orf72 ALS/FTD

NIH-funded research St. Joseph's Hospital and Medical Center · NIH-10897724

This study is looking at how certain brain cells called microglia might affect the progression of ALS and frontotemporal dementia in people with a specific genetic mutation, to help us understand how these conditions develop and find new ways to treat them.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionSt. Joseph's Hospital and Medical Center NIH-funded
Lab location1 site (Phoenix, United States)
Project IDNIH-10897724 on NIH RePORTER

What this research studies

This research investigates the role of microglia, a type of immune cell in the brain, in the development of amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD), particularly in patients with the C9orf72 genetic mutation. The study aims to understand how microglia activation correlates with cognitive decline and FTD-like symptoms in ALS patients. By examining brain tissue from affected individuals, researchers will explore the differences in microglial function based on genetic factors and how these cells interact with neurons. This could lead to insights into the mechanisms of disease progression and potential therapeutic targets.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with ALS or FTD, particularly those with the C9orf72 genetic mutation.

Not a fit: Patients with other forms of dementia or neurological disorders unrelated to ALS or FTD may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments that target microglial dysfunction, potentially improving outcomes for patients with ALS and FTD.

How similar studies have performed: Previous research has shown that targeting microglial activation can have beneficial effects in other neurodegenerative diseases, suggesting potential for success in this area as well.

Where this research is happening

Phoenix, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Alzheimer disease dementiaAlzheimer syndromeAlzheimer's DiseaseAlzheimer's disease and related dementiaAlzheimer's disease and related disorders
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.