Understanding how methotrexate affects brain health in children with cancer

Mechanistic Study of Methotrexate-Induced Oxidative Distress in Neurons and the CSF

NIH-funded research Boston Children's Hospital · NIH-11089458

This study is looking at how the chemotherapy drug methotrexate, used to treat childhood leukemia, might affect thinking and memory, often called 'chemobrain', and aims to find ways to help prevent or treat these side effects for kids undergoing treatment.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionBoston Children's Hospital NIH-funded
Lab location1 site (Boston, United States)
Project IDNIH-11089458 on NIH RePORTER

What this research studies

This research investigates the neurocognitive side effects of methotrexate, a common chemotherapy drug used in treating childhood leukemia. It focuses on understanding the molecular mechanisms behind chemotherapy-induced cognitive impairments, often referred to as 'chemobrain'. By analyzing cerebrospinal fluid from treated patients and animal models, the study aims to identify metabolic changes and oxidative distress caused by the drug. The ultimate goal is to develop preventive strategies or treatments to mitigate these harmful effects on brain function.

Who could benefit from this research

Good fit: Ideal candidates for this research are pediatric cancer patients receiving methotrexate as part of their treatment regimen.

Not a fit: Patients who are not undergoing chemotherapy or those receiving treatments other than methotrexate may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to improved strategies for preventing or treating cognitive impairments in children undergoing chemotherapy.

How similar studies have performed: Previous research has shown promising results in understanding chemotherapy-related cognitive impairments, but this specific focus on methotrexate's mechanisms is relatively novel.

Where this research is happening

Boston, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.