Understanding how lysosomal dysfunctions affect Frontotemporal Dementia

Development of Mass Spectrometry Strategies to Decipher Dynamic Lysosomal Dysfunctions in Frontotemporal Dementia

NIH-funded research Univ of Maryland, College Park · NIH-11249844

This study is looking at a protein called progranulin to see how its absence affects brain cells in people with Frontotemporal Dementia, with the hope of finding new ways to treat the condition.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniv of Maryland, College Park NIH-funded
Lab location1 site (College Park, United States)
Project IDNIH-11249844 on NIH RePORTER

What this research studies

This research investigates the role of progranulin, a protein linked to lysosomal function, in Frontotemporal Dementia (FTD). By using advanced mass spectrometry techniques, the study aims to analyze how the absence of progranulin affects lysosomal activities in neurons derived from human stem cells. The researchers will develop methods to observe and quantify the interactions and functions of lysosomes in these neurons, ultimately seeking to identify potential therapeutic targets for FTD. This work could lead to a better understanding of the disease mechanisms and pave the way for new treatment strategies.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with Frontotemporal Dementia, particularly those with mutations in the GRN gene.

Not a fit: Patients with Frontotemporal Dementia who do not have GRN mutations or other related lysosomal dysfunctions may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new therapeutic targets and strategies for treating Frontotemporal Dementia.

How similar studies have performed: While lysosomal dysfunctions have been studied in various neurodegenerative diseases, this specific approach using mass spectrometry in FTD is relatively novel and has not been extensively tested.

Where this research is happening

College Park, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-09 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.