Understanding how human genes function through advanced genetic techniques

Multi-omic phenotyping of human transcriptional regulators

['FUNDING_U01'] · JACKSON LABORATORY · NIH-10927399

This study is exploring how our genes work by using special tools to turn off specific genes and see how cells behave over time, which will help us understand more about gene functions and how they relate to health and disease.

Quick facts

Phase['FUNDING_U01']
Study typeNih_funding
SexAll
SponsorJACKSON LABORATORY (nih funded)
Locations1 site (BAR HARBOR, UNITED STATES)
Trial IDNIH-10927399 on ClinicalTrials.gov

What this research studies

This research investigates the functions of human genes by using advanced genetic techniques such as CRISPR to create targeted gene knockouts and knockdowns. By applying these techniques, researchers will profile the molecular characteristics of cells over time, using both bulk and single-cell RNA sequencing. The goal is to catalog the functions of every human gene, particularly focusing on transcription factors that play a crucial role in regulating cell behavior. This comprehensive approach aims to provide a deeper understanding of gene function and its implications for health and disease.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals with genetic conditions or those interested in the genetic basis of diseases.

Not a fit: Patients without genetic conditions or those not interested in genetic research may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to significant advancements in understanding genetic diseases and developing targeted therapies.

How similar studies have performed: Other research has shown success with similar genetic perturbation approaches, indicating a promising avenue for understanding gene function.

Where this research is happening

BAR HARBOR, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.