Understanding how genetic variations affect brain function in Alzheimer's disease

Modeling the impact of regulatory and splicing variants on cellular function in Alzheimer's disease

NIH-funded research Icahn School of Medicine at Mount Sinai · NIH-11051243

This study is looking at how differences in our genes might affect brain health and contribute to Alzheimer's disease, so that people can better understand their own risk and find new ways to help prevent or treat the condition.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionIcahn School of Medicine at Mount Sinai NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11051243 on NIH RePORTER

What this research studies

This research investigates the role of genetic variations in the development of Alzheimer's disease (AD), focusing on how these variations impact cellular functions related to brain health. By analyzing genetic data and using advanced techniques like human induced pluripotent stem cells (hiPSCs), the team aims to identify specific genetic factors that contribute to AD. Patients may benefit from insights into how their genetic makeup influences their risk for AD and potential new therapeutic targets. The study employs a combination of statistical analysis and cellular models to explore these genetic influences.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals with a family history of Alzheimer's disease or those showing early signs of cognitive decline.

Not a fit: Patients with non-genetic forms of dementia or those without any familial link to Alzheimer's disease may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new strategies for preventing or treating Alzheimer's disease by targeting specific genetic factors.

How similar studies have performed: Previous research has shown promise in understanding genetic contributions to Alzheimer's disease, suggesting that this approach could yield valuable insights.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions age associated neurodegenerative diseaseage associated neurodegenerative disorderage dependent neurodegenerative diseaseage dependent neurodegenerative disorder
Last reviewed 2026-06-09 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.