Understanding how FMRP affects gene expression in Fragile X Syndrome

FMRP Regulation of Gene Expression

NIH-funded research Univ of Massachusetts Med Sch Worcester · NIH-10695214

This study is looking at how a protein called FMRP works in the brains of people with Fragile X Syndrome to understand why they might have extra protein production, which can cause challenges, and it hopes to find new ways to help those affected by this condition.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniv of Massachusetts Med Sch Worcester NIH-funded
Lab location1 site (Worcester, United States)
Project IDNIH-10695214 on NIH RePORTER

What this research studies

This research investigates the role of the FMRP protein in regulating gene expression, particularly in individuals with Fragile X Syndrome, a genetic condition that can lead to cognitive and developmental challenges. By examining how FMRP interacts with ribosomes and mRNA in the brain, the study aims to uncover the mechanisms behind excessive protein synthesis that contributes to the symptoms of this disorder. The approach involves advanced techniques like ribosome profiling to identify specific mRNAs affected by FMRP, which could lead to new insights into treatment strategies for those impacted by Fragile X Syndrome.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with Fragile X Syndrome or related genetic conditions who are over 21 years old.

Not a fit: Patients without Fragile X Syndrome or those who do not have related genetic conditions may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to improved understanding and potential therapies for individuals with Fragile X Syndrome and related disorders.

How similar studies have performed: Previous research has shown promising results in understanding the role of FMRP in Fragile X Syndrome, indicating that this approach has potential for significant advancements.

Where this research is happening

Worcester, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.