Understanding how cell changes lead to aggressive leukemia

The role for phase separation in oncogenesis and aberrant chromatin looping formation

['FUNDING_R01'] · DUKE UNIVERSITY · NIH-11116919

This project looks into how specific gene changes in cells contribute to aggressive forms of acute myeloid leukemia (AML) in patients.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorDUKE UNIVERSITY (nih funded)
Locations1 site (DURHAM, UNITED STATES)
Trial IDNIH-11116919 on ClinicalTrials.gov

What this research studies

We know that certain changes in a gene called NUP98 are common in patients with acute myeloid leukemia (AML) and often lead to poor outcomes. This project explores how these NUP98 gene changes cause cells to form abnormal structures, similar to oil and water separating, which then drives the development of aggressive AML. By understanding this process, we hope to uncover new ways to stop the disease from progressing. This work focuses on how these gene changes affect the way DNA is organized and expressed, leading to cancer growth.

Who could benefit from this research

Good fit: This research is most relevant to patients diagnosed with acute myeloid leukemia, particularly those whose disease involves rearrangements of the NUP98 gene.

Not a fit: Patients with other types of leukemia or those whose AML does not involve NUP98 gene rearrangements may not directly benefit from this specific research.

Why it matters

Potential benefit: If successful, this research could lead to new treatment strategies for patients with aggressive forms of acute myeloid leukemia, especially those with NUP98 gene rearrangements.

How similar studies have performed: This work builds on the researchers' own preliminary findings, suggesting a novel mechanism for leukemia development that has not been widely explored.

Where this research is happening

DURHAM, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.