Understanding how abnormal Gas activation affects blood cancer

Mechanisms and targeting of aberrant Gas activation in myeloid neoplasms

NIH-funded research Icahn School of Medicine at Mount Sinai · NIH-11056848

This study is looking into the genetic changes that cause blood cancers like acute myeloid leukemia (AML) and myelodysplastic syndromes (MDS) to help find new treatment options for patients.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionIcahn School of Medicine at Mount Sinai NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11056848 on NIH RePORTER

What this research studies

This research investigates the mechanisms behind myeloid neoplasms, particularly focusing on acute myeloid leukemia (AML) and myelodysplastic syndromes (MDS). By utilizing advanced techniques like CRISPR gene editing and RNA sequencing, the study aims to identify specific genetic mutations that lead to abnormal cell behavior. The goal is to uncover potential therapeutic targets that could lead to effective treatments for patients suffering from these aggressive blood cancers. Patients may benefit from insights into new treatment strategies based on the genetic underpinnings of their disease.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with acute myeloid leukemia or myelodysplastic syndromes, particularly those with specific genetic mutations.

Not a fit: Patients with other types of leukemia or those without the identified genetic mutations may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to the development of targeted therapies for patients with acute myeloid leukemia and myelodysplastic syndromes.

How similar studies have performed: Previous research has shown promise in targeting genetic mutations in blood cancers, indicating that this approach could yield significant advancements.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.