Understanding how a specific gene affects a type of nerve sheath tumor in patients with neurofibromatosis type 1.

Regulation of MPNST pathogenesis by Chromosome 8 gene, UBR5

['FUNDING_R01'] · WASHINGTON UNIVERSITY · NIH-11012336

This study is looking at how a gene called UBR5 affects the growth of a type of cancer called malignant peripheral nerve sheath tumors in people with neurofibromatosis type 1, with the hope of finding new treatments to help those battling this tough disease.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorWASHINGTON UNIVERSITY (nih funded)
Locations1 site (SAINT LOUIS, UNITED STATES)
Trial IDNIH-11012336 on ClinicalTrials.gov

What this research studies

This research investigates the role of the UBR5 gene in the development of malignant peripheral nerve sheath tumors (MPNST) in patients with neurofibromatosis type 1 (NF1). By using patient-derived xenografts, the study aims to understand how changes in chromosome 8 contribute to tumor growth and survival. The researchers will explore when these genetic changes occur during tumor progression and how targeting UBR5 could lead to new treatment options. This approach may help identify more effective therapies for patients suffering from this aggressive cancer.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with neurofibromatosis type 1 who are at risk of developing malignant peripheral nerve sheath tumors.

Not a fit: Patients without neurofibromatosis type 1 or those who do not have MPNST may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new targeted therapies that improve survival rates for patients with MPNST.

How similar studies have performed: Previous research has shown promising results in targeting genetic abnormalities in cancer, suggesting that this approach could be effective.

Where this research is happening

SAINT LOUIS, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: anti-cancer therapy, cancer predisposition

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.