Understanding ATRX in Brain Development

CTCF-dependent mechanisms of ATRX in neuronal differentiation

NIH-funded research Wistar Institute · NIH-11128626

This research explores how a protein called ATRX works in brain development and how changes in this protein can lead to ATRX syndrome.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionWistar Institute NIH-funded
Lab location1 site (Philadelphia, United States)
Project IDNIH-11128626 on NIH RePORTER

What this research studies

We are learning more about a protein called ATRX, which is essential for the healthy development of brain cells. When ATRX has mutations, it can cause ATRX syndrome, leading to intellectual disability and other developmental challenges. Our work focuses on how different types of ATRX mutations affect a key process in the brain and how they might lead to varying symptoms. We are particularly interested in how ATRX interacts with another important protein called CTCF, which helps organize our genetic material.

Who could benefit from this research

Good fit: This foundational research is for patients and families affected by ATRX syndrome who are interested in the underlying causes of the condition and future treatment possibilities.

Not a fit: Patients without ATRX syndrome or related neurodevelopmental conditions may not directly benefit from this specific research.

Why it matters

Potential benefit: If successful, this work could lead to a better understanding of ATRX syndrome, potentially paving the way for new ways to help individuals affected by this condition.

How similar studies have performed: While ATRX's general roles are known, this research is novel in investigating the specific link between different mutation types and their effects on brain development, building on promising preliminary data.

Where this research is happening

Philadelphia, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.