Understanding and Overcoming Drug Resistance in Medulloblastoma

Transporters and Medulloblastoma

NIH-funded research St. Jude Children's Research Hospital · NIH-11045634

This work explores new ways to help children with medulloblastoma by making their chemotherapy more effective against the tumor.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionSt. Jude Children's Research Hospital NIH-funded
Lab location1 site (Memphis, United States)
Project IDNIH-11045634 on NIH RePORTER

What this research studies

Medulloblastoma, a common and serious brain cancer in children, is often hard to treat because chemotherapy drugs struggle to reach the tumor due to natural barriers in the brain. This project focuses on a specific barrier protein called ABCG2, which is highly active in aggressive forms of medulloblastoma and pushes chemotherapy drugs out of tumor cells. Researchers have found a new way to block ABCG2 by removing it from the cell surface, which could allow more chemotherapy to reach the cancer. This approach aims to improve how well current treatments work for children facing this challenging disease.

Who could benefit from this research

Good fit: This research is primarily focused on understanding and treating medulloblastoma, especially the aggressive Group 3 subtype, which affects children and young adults.

Not a fit: Patients with other types of cancer or those whose medulloblastoma does not involve the ABCG2 transporter may not directly benefit from this specific approach.

Why it matters

Potential benefit: If successful, this work could lead to more effective chemotherapy treatments for children with medulloblastoma, potentially improving their survival and quality of life.

How similar studies have performed: While the concept of targeting drug transporters is known, this specific approach of promoting ABCG2 membrane retrieval with a novel inhibitor appears to be a new and promising strategy.

Where this research is happening

Memphis, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.