Targeting the vitamin B6 pathway in acute myeloid leukemia

Characterizing vitamin B6 pathway dependency in acute myeloid leukemia

['FUNDING_R37'] · COLD SPRING HARBOR LABORATORY · NIH-11257716

This research looks at whether blocking the vitamin B6 pathway can help treat people with acute myeloid leukemia.

Quick facts

Phase['FUNDING_R37']
Study typeNih_funding
SexAll
SponsorCOLD SPRING HARBOR LABORATORY (nih funded)
Locations1 site (COLD SPRING HARBOR, UNITED STATES)
Trial IDNIH-11257716 on ClinicalTrials.gov

What this research studies

From a patient perspective, scientists will examine leukemia cells and bone marrow samples to find which enzymes in the vitamin B6 pathway AML cells depend on. They will use genetic tools such as CRISPR screens and laboratory models to turn off those genes and see how leukemia cells respond compared with normal blood stem cells. The team will test drug-like approaches and combinations that inhibit key enzymes to identify potential drug targets. Successful targets would then be moved toward further preclinical testing and possible early-phase patient studies.

Who could benefit from this research

Good fit: Adults with acute myeloid leukemia, especially those with relapsed or refractory disease or whose leukemia shows signs of vitamin B6 pathway activity, would be the most relevant candidates.

Not a fit: People with other cancers, patients whose leukemia does not rely on the vitamin B6 pathway, or those seeking immediate clinical treatment are unlikely to receive direct benefit from this lab-focused project.

Why it matters

Potential benefit: If successful, this work could uncover new targeted therapies that kill AML cells while sparing normal blood cells, potentially improving effectiveness and reducing toxicity.

How similar studies have performed: This is a novel approach with promising laboratory evidence for vitamin B6 dependency but it has not yet produced proven patient treatments.

Where this research is happening

COLD SPRING HARBOR, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.