Targeting the metabolic needs of children with acute myeloid leukemia

Exploiting the Metabolic Dependencies of Pediatric AML

NIH-funded research Baylor College of Medicine · NIH-11093346

This study is looking at how a safe medication called atovaquone can help improve treatment for kids with acute myeloid leukemia (AML) by targeting the way leukemia cells use energy, with the hope of making treatments more effective and less harmful.

Quick facts

Grant typeCareer grant
Study typeNIH-funded research
Funding institutionBaylor College of Medicine NIH-funded
Lab location1 site (Houston, United States)
Project IDNIH-11093346 on NIH RePORTER

What this research studies

This research focuses on improving treatment outcomes for pediatric patients with acute myeloid leukemia (AML) by identifying and targeting the specific metabolic dependencies of leukemia cells. The approach involves using a well-tolerated drug called atovaquone to assess its effectiveness in treating AML and understanding how it affects leukemia cell metabolism. The research includes a clinical trial to incorporate atovaquone into standard treatment regimens and collect biospecimens for further analysis. The ultimate goal is to enhance cure rates while minimizing treatment-related toxicities for young patients.

Who could benefit from this research

Good fit: Ideal candidates for this research are pediatric patients aged 0-11 years who have been diagnosed with acute myeloid leukemia.

Not a fit: Patients with other types of leukemia or those outside the pediatric age range may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective and less toxic treatment options for children suffering from acute myeloid leukemia.

How similar studies have performed: Previous research has shown promising results in targeting metabolic pathways in leukemia, suggesting that this approach could be effective.

Where this research is happening

Houston, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.