Targeting a specific pathway in aggressive nerve tumors associated with NF1.

Understanding and targeting MAPK pathway activation in NF1-deficient malignant peripheral nerve sheath tumor (MPNST)

NIH-funded research Sloan-Kettering Inst Can Research · NIH-11034089

This study is looking at how certain genetic changes in aggressive tumors related to neurofibromatosis type 1 can make them hard to treat, and it’s testing a new combination therapy that might help improve treatment for patients with these tumors.

Quick facts

Grant typeU01 cooperative agreement
Study typeNIH-funded research
Funding institutionSloan-Kettering Inst Can Research NIH-funded
Lab location1 site (New York, United States)
Project IDNIH-11034089 on NIH RePORTER

What this research studies

This research focuses on malignant peripheral nerve sheath tumors (MPNSTs), which are aggressive cancers often linked to neurofibromatosis type 1 (NF1). The study aims to understand how certain genetic alterations contribute to the resistance of these tumors to existing treatments. By analyzing tumor samples and using preclinical models, researchers are investigating a novel combination therapy that targets specific pathways involved in tumor growth. This approach could potentially improve treatment outcomes for patients with NF1-related MPNSTs.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with NF1 and malignant peripheral nerve sheath tumors.

Not a fit: Patients with MPNSTs not associated with NF1 or those with other types of tumors may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatment options for patients suffering from NF1-related malignant peripheral nerve sheath tumors.

How similar studies have performed: Previous research has shown promise in targeting similar pathways in other tumor types, suggesting potential for success in this novel approach.

Where this research is happening

New York, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.