Targeting a specific enzyme to treat liver cancer

Ornithine Aminotransferase Inactivation, a New Approach for Treatment of Cancers

NIH-funded research Northwestern University · NIH-11049021

This study is looking at a special enzyme that's found in high amounts in liver cancer to create new treatments that can better target the cancer while causing fewer side effects for patients.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionNorthwestern University NIH-funded
Lab location1 site (Chicago, UNITED STATES)
Project IDNIH-11049021 on NIH RePORTER

What this research studies

This research investigates the role of ornithine aminotransferase (OAT), an enzyme that is overexpressed in liver cancer, specifically hepatocellular carcinoma (HCC). The approach involves using computer modeling to design new compounds that can selectively inhibit OAT, potentially leading to more effective cancer treatments with fewer side effects. The researchers will modify existing compounds to enhance their effectiveness and test them against cancer cell lines that overexpress OAT. The goal is to develop targeted therapies that can improve outcomes for patients with liver cancer.

Who could benefit from this research

Good fit: Ideal candidates for this research are patients diagnosed with hepatocellular carcinoma who may benefit from targeted cancer therapies.

Not a fit: Patients with cancers that do not involve the overexpression of ornithine aminotransferase may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new, more effective treatments for liver cancer that minimize side effects.

How similar studies have performed: While targeting specific enzymes in cancer treatment is a growing field, this particular approach to inhibit OAT is novel and has not been extensively tested in clinical settings.

Where this research is happening

Chicago, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions anti-cancer therapy
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.