Targeting a gene to improve brain cell function in Alzheimer's disease

siRNA-mediated Knockdown of INPP5D to Modulate Microglia Activity for the Treatment of Alzheimer's Disease

['FUNDING_R01'] · INDIANA UNIVERSITY INDIANAPOLIS · NIH-11107595

This study is looking at how a gene called INPP5D affects brain immune cells in people with Alzheimer's, and by tweaking this gene, researchers hope to improve these cells' function and slow down memory loss, which could lead to new treatments for patients.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorINDIANA UNIVERSITY INDIANAPOLIS (nih funded)
Locations1 site (INDIANAPOLIS, UNITED STATES)
Trial IDNIH-11107595 on ClinicalTrials.gov

What this research studies

This research investigates the role of a specific gene, INPP5D, in the activity of brain immune cells called microglia, which are crucial in Alzheimer's disease. By using a technique called siRNA to reduce the expression of this gene, the study aims to enhance microglial function and potentially slow down the progression of Alzheimer's. The research involves both genetic analysis and mouse models to understand how modifying this gene can impact cognitive decline and amyloid plaque accumulation. Patients may benefit from new therapeutic strategies that arise from this approach.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with Alzheimer's disease or those at risk due to genetic factors.

Not a fit: Patients with other forms of dementia unrelated to Alzheimer's disease may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatments for Alzheimer's disease that improve cognitive function and reduce disease progression.

How similar studies have performed: Previous research has shown promise in targeting microglial function for Alzheimer's treatment, indicating that this approach may lead to significant advancements.

Where this research is happening

INDIANAPOLIS, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: Alzheimer disease dementia

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.