Stopping Nerve Tumors in NF1 Patients

TAM receptor inhibition in NF1-associated peripheral nerve sheath tumors

NIH-funded research Indiana University Indianapolis · NIH-11101324

This research explores new ways to stop nerve tumors from growing and becoming cancerous in people with Neurofibromatosis type 1 (NF1).

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionIndiana University Indianapolis NIH-funded
Lab location1 site (Indianapolis, United States)
Project IDNIH-11101324 on NIH RePORTER

What this research studies

Neurofibromatosis type 1 (NF1) is a genetic condition that often leads to nerve tumors called plexiform neurofibromas, which can sometimes turn into a very aggressive cancer. This project uses advanced mouse models that closely mimic how these tumors develop and progress in humans. Researchers have identified specific targets, called TAM family kinases, that play a key role in these tumors. They are exploring a drug called cabozantinib, which blocks these targets, and has shown promise in delaying or preventing tumor progression in these models, with some early clinical observations also supporting this approach. The goal is to understand how this drug works to prevent these tumors from becoming cancerous.

Who could benefit from this research

Good fit: Patients with Neurofibromatosis type 1 (NF1) who have plexiform neurofibromas or atypical neurofibromas that are at risk of becoming cancerous are the focus of this research.

Not a fit: Patients without NF1 or those whose tumors have already progressed to advanced, aggressive forms might not directly benefit from this specific preventative approach.

Why it matters

Potential benefit: If successful, this research could lead to new treatments that prevent or significantly delay the progression of NF1-related nerve tumors into life-threatening cancers.

How similar studies have performed: Preliminary clinical data and preclinical models suggest this approach has shown some promise in delaying tumor progression.

Where this research is happening

Indianapolis, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.