Predicting methotrexate-related brain side effects in children with ALL

A Systems Epidemiology Approach for Predicting Methotrexate Neurotoxicity in Pediatric Acute Leukemia

NIH-funded research Baylor College of Medicine · NIH-11305990

This project works to predict which children and teens with acute lymphoblastic leukemia will develop methotrexate-related neurotoxicity using clinical signs and biological data.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionBaylor College of Medicine NIH-funded
Lab location1 site (Houston, United States)
Project IDNIH-11305990 on NIH RePORTER

What this research studies

Researchers will combine medical records, reports of early neurological symptoms, and biological samples such as blood and genetic tests to build a predictive model for methotrexate neurotoxicity. The team focuses on children and adolescents with acute lymphoblastic leukemia and is paying special attention to why Latino patients may face higher risk. The approach links symptom tracking with lab-based biomarkers to identify host factors that signal increased toxicity risk. Study findings could inform closer monitoring or treatment adjustments to prevent severe brain side effects.

Who could benefit from this research

Good fit: Ideal participants are children and adolescents diagnosed with acute lymphoblastic leukemia who are receiving methotrexate, with particular emphasis on enrolling Latino patients.

Not a fit: Patients not treated with methotrexate, adults, people with other cancers, or those whose neurotoxicity occurs long after therapy may not benefit directly from this project.

Why it matters

Potential benefit: If successful, this work could help doctors identify at-risk children earlier so treatments or monitoring can be adjusted to prevent or reduce methotrexate brain side effects and improve outcomes.

How similar studies have performed: Previous work from the team shows early mild-to-moderate neurological symptoms often precede clinical methotrexate neurotoxicity, but comprehensive predictive models integrating clinical and biological data remain novel and require validation.

Where this research is happening

Houston, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.