PFKFB3 and scarring beneath the retina in wet age-related macular degeneration

RPE PFKFB3 in subretinal fibrosis

NIH-funded research State University New York Stony Brook · NIH-11402090

This work looks at whether blocking a cell enzyme called PFKFB3 in retinal pigment epithelial cells can reduce scarring beneath the retina and help people with wet age-related macular degeneration.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionState University New York Stony Brook NIH-funded
Lab location1 site (Stony Brook, United States)
Project IDNIH-11402090 on NIH RePORTER

What this research studies

Researchers are studying a cell enzyme (PFKFB3) in retinal pigment epithelial (RPE) cells that may drive the scarring that follows abnormal blood vessel growth in wet AMD. They will use lab cell experiments and two mouse models — laser-induced choroidal neovascularization and Vldlr knockout mice that develop spontaneous subretinal fibrosis — to remove PFKFB3 specifically in RPE cells and observe effects on scarring and visual function. The team will measure inflammatory and fibrotic signals, cellular transitions (like epithelial-to-mesenchymal changes), retinal structure, and functional readouts, building on earlier findings that PFKFB3 alters metabolism and promotes pro-fibrotic behavior. Results are intended to identify whether targeting PFKFB3 could be a route to therapies that stop or slow subretinal scar formation.

Who could benefit from this research

Good fit: People with neovascular (wet) age-related macular degeneration, particularly those with choroidal neovascularization or early signs of subretinal fibrosis, would be the most relevant candidates for future therapies.

Not a fit: People with dry (atrophic) AMD or those who already have long-standing, fully formed disciform scars are unlikely to benefit from therapies aimed at preventing fibrosis.

Why it matters

Potential benefit: Could point to new treatments that prevent or reduce scarring beneath the retina and help preserve vision in people with wet AMD.

How similar studies have performed: Related laboratory studies have linked PFKFB3 to fibrotic and inflammatory changes in other tissues, but applying PFKFB3-targeting to subretinal fibrosis is a novel approach.

Where this research is happening

Stony Brook, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.