Peptide vaccine targeting CMV for children with high-grade glioma, DIPG, and recurrent medulloblastoma

Phase 2 trial of a novel peptide vaccine targeting CMV antigen for newly diagnosed pediatric high grade glioma and diffuse intrinsic pontine glioma and recurrent medulloblastoma

NIH-funded research Duke University · NIH-11177623

This vaccine trains the immune system to target a viral protein (CMV pp65) that is often found in certain pediatric brain tumors to help slow or shrink the tumor.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionDuke University NIH-funded
Lab location1 site (Durham, United States)
Project IDNIH-11177623 on NIH RePORTER

What this research studies

You would receive a series of peptide vaccine injections called PEP-CMV designed to teach your immune system to recognize the CMV pp65 protein found in many high-grade gliomas, DIPG, and recurrent medulloblastomas. The trial enrolls children and young adults with newly diagnosed HGG or DIPG or with recurrent medulloblastoma and follows them over time with blood tests and MRI scans. The team previously gave this vaccine in a Phase I group and saw immune responses in most patients and some cases of stable disease or partial tumor shrinkage without severe toxicities. Study doctors will closely monitor safety, immune response markers, and tumor imaging during and after the vaccine series.

Who could benefit from this research

Good fit: Children and young adults with newly diagnosed high-grade glioma or DIPG, or with recurrent medulloblastoma who meet the trial's medical criteria and can travel for vaccinations and follow-up are ideal candidates.

Not a fit: Patients whose tumors do not express the CMV pp65 protein, who are medically unstable, or who have immune conditions that prevent vaccination may not benefit or be eligible.

Why it matters

Potential benefit: If successful, the vaccine could help the immune system slow tumor growth or shrink tumors, potentially prolonging survival and reducing reliance on more toxic treatments.

How similar studies have performed: Early Phase I results showed immune responses in about 75% of participants and some disease stabilization or partial responses, so the approach is promising but still experimental.

Where this research is happening

Durham, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.