New treatments for neuroblastoma in children

Novel Therapeutic Approaches for the Treatment of Neuroblastoma

['FUNDING_R01'] · ST. JUDE CHILDREN'S RESEARCH HOSPITAL · NIH-10977341

This study is looking for new ways to treat neuroblastoma, a tough cancer that mostly affects kids, by exploring how certain gene changes can be used to make treatments more effective.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorST. JUDE CHILDREN'S RESEARCH HOSPITAL (nih funded)
Locations1 site (MEMPHIS, UNITED STATES)
Trial IDNIH-10977341 on ClinicalTrials.gov

What this research studies

This research focuses on developing innovative therapies for neuroblastoma, a type of aggressive cancer that primarily affects children. The team is investigating the relationship between specific genetic mutations, particularly the MYCN oncogene and ATRX tumor-suppressor gene, to identify how these mutations can be targeted for treatment. By using human cell lines and mouse models, they aim to exploit the vulnerabilities created by these mutations to improve patient outcomes. The approach includes using targeted therapies that disrupt the cancer cells' ability to survive and grow.

Who could benefit from this research

Good fit: Ideal candidates for this research are children aged 0-11 years diagnosed with high-risk or recurrent neuroblastoma.

Not a fit: Patients with neuroblastoma who do not have MYCN amplification or ATRX mutations may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatments for children with high-risk neuroblastoma, potentially improving survival rates and quality of life.

How similar studies have performed: Previous research has shown promising results in targeting genetic vulnerabilities in cancers, suggesting that this approach could be effective for neuroblastoma as well.

Where this research is happening

MEMPHIS, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.