New treatment approach for myelodysplastic syndrome and acute myeloid leukemia

A novel approach for treating myelodysplastic syndrome (MDS) and acute myeloid leukemia (AML)

NIH-funded research Avantgen, INC. · NIH-11189625

This project aims to develop a new antibody-based therapy to help people with MDS or AML, especially older or frail patients who cannot tolerate high-dose chemotherapy.

Quick facts

Grant typeSbir 2 grant
Study typeNIH-funded research
Funding institutionAvantgen, INC. NIH-funded
Lab location1 site (San Diego, United States)
Project IDNIH-11189625 on NIH RePORTER

What this research studies

Many people with MDS rely on blood transfusions and older medications, and about one-third progress to AML, which is particularly hard to treat in older or unfit patients. This project is developing an antibody-based therapy designed to target and kill abnormal blood precursor cells that drive MDS and AML. The team will manufacture the therapeutic agent and perform laboratory and preclinical testing as steps toward giving the treatment to patients. If human testing occurs, participants would receive the experimental therapy and have regular monitoring for safety and response.

Who could benefit from this research

Good fit: Adults with myelodysplastic syndrome or acute myeloid leukemia, especially older or medically unfit patients and those with relapsed or treatment‑resistant disease, would be the most likely candidates.

Not a fit: Patients who are candidates for curative high‑dose induction chemotherapy and hematopoietic stem cell transplant may not receive benefit from this experimental approach.

Why it matters

Potential benefit: If successful, this could offer a new treatment option that reduces transfusion needs, delays progression to AML, and improves outcomes for patients who cannot undergo intensive chemotherapy.

How similar studies have performed: Targeted small-molecule drugs have helped some AML subgroups but tend to have high relapse rates, while antibody-based treatments for AML/MDS are newer and remain under active investigation.

Where this research is happening

San Diego, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.