New treatment approach for a type of brain tumor in children

Combination metabolic therapy for diffuse midline glioma

NIH-funded research University of California, San Francisco · NIH-10943578

This study is looking at a type of brain tumor in kids called diffuse midline gliomas, and it's trying to find ways to target a specific genetic change in these tumors to create better treatments that could help shrink the tumors and improve survival.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of California, San Francisco NIH-funded
Lab location1 site (San Francisco, United States)
Project IDNIH-10943578 on NIH RePORTER

What this research studies

This research focuses on diffuse midline gliomas (DMGs), aggressive brain tumors in children that have a poor prognosis. The study aims to identify specific vulnerabilities caused by a genetic mutation (H3K27M) in these tumors, which can lead to targeted therapies. By inhibiting certain metabolic pathways that the tumors rely on for growth, the researchers hope to induce tumor regression and improve survival rates. The approach includes using advanced imaging techniques to monitor treatment effects in real-time.

Who could benefit from this research

Good fit: Ideal candidates for this research are children diagnosed with diffuse midline gliomas, particularly those with the H3K27M mutation.

Not a fit: Patients with other types of brain tumors or those without the H3K27M mutation may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatments for children with diffuse midline gliomas, potentially improving survival rates and quality of life.

How similar studies have performed: Other research has shown promising results in targeting metabolic pathways in cancer, suggesting that this approach could be effective for treating DMGs as well.

Where this research is happening

San Francisco, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.