Mycophenolate mofetil plus temozolomide for newly diagnosed glioblastoma (early-phase)

A Phase 1 Adaptive Dose Escalation Study of Mycophenolate Mofetil in Combination with Temozolomide for Patients with Newly Diagnosed Glioblastoma

NIH-funded research Northwestern University · NIH-11187084

This early-phase trial tests whether adding the drug mycophenolate mofetil to standard temozolomide chemotherapy is safe and tolerable for people newly diagnosed with glioblastoma.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionNorthwestern University NIH-funded
Lab location1 site (Chicago, United States)
Project IDNIH-11187084 on NIH RePORTER

What this research studies

If you are newly diagnosed with glioblastoma and receiving standard surgery and temozolomide, this project adds mycophenolate mofetil and uses an adaptive dose-escalation plan to find a safe dose. Doctors will monitor side effects closely and may collect blood and tumor-related samples to look for biomarkers linked to how the drugs work. The team is building on lab findings about cancer cell purine metabolism to see whether this combination can reduce treatment resistance. Participation will involve regular clinic visits, scans, and blood tests while dosing is adjusted to balance safety and potential benefit.

Who could benefit from this research

Good fit: Adults with newly diagnosed glioblastoma who are planning to receive temozolomide and meet medical safety criteria would be the ideal candidates.

Not a fit: People with recurrent glioblastoma, those unable to tolerate immunosuppressive medications, or pediatric patients are unlikely to benefit from this protocol.

Why it matters

Potential benefit: If successful, the combination could make standard chemotherapy work better and reduce the chance of tumor recurrence.

How similar studies have performed: This approach is largely novel in glioblastoma: supporting lab and preclinical data exist, but human data are limited and this is an early-phase safety-focused effort.

Where this research is happening

Chicago, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.