MTSS1 and heart muscle health

MTSS1 in myocardial disease

NIH-funded research University of Pennsylvania · NIH-11230037

This project looks at how changes in the MTSS1 gene affect heart size and the risk of heart muscle disease, with effects seen mainly in adult women.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Pennsylvania NIH-funded
Lab location1 site (Philadelphia, United States)
Project IDNIH-11230037 on NIH RePORTER

What this research studies

Researchers study how genetic changes that lower MTSS1 in heart muscle change heart size and function. They combine lab experiments in mice with analysis of human heart MRI data from the UK Biobank to compare effects in men and women. Early results show MTSS1 reduction helped heart function in female mice and that genetic variants linked to lower MTSS1 associate with better heart measurements in women but not men. The team will fine-map the gene region and study mechanisms to understand how MTSS1 might be used to protect people from dilated cardiomyopathy.

Who could benefit from this research

Good fit: Adults—particularly women—with or at risk for dilated cardiomyopathy or who carry relevant genetic variants would be most relevant.

Not a fit: People without heart muscle problems or without the relevant genetic risk factors may not see direct benefit from this research.

Why it matters

Potential benefit: If successful, this work could point to new ways to prevent or treat heart muscle disease that are tailored by sex.

How similar studies have performed: Prior animal experiments and human genetic analyses from this team suggest MTSS1 reduction can be protective in females, so these findings are promising but still need translation.

Where this research is happening

Philadelphia, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.