Mouse models carrying human inhibitory brain cells from specific brain regions

Brain-region-specific humanized cortical interneuron mice

NIH-funded research Rutgers Biomedical and Health Sciences · NIH-11309691

This project puts human inhibitory brain cells into mice to learn how changes in those cells may contribute to autism.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionRutgers Biomedical and Health Sciences NIH-funded
Lab location1 site (Newark, UNITED STATES)
Project IDNIH-11309691 on NIH RePORTER

What this research studies

Researchers grow human cortical interneurons from stem cells, including cells derived from people with and without autism, and transplant them into specific regions of mouse brains to create 'humanized' models. They include other human support cells like astrocytes so the transplanted cells live in a more realistic brain environment. The team then studies how these human cells change brain circuit activity and behaviors linked to autism. This lets them observe the effects of human genetic differences in a living brain context that rodent-only models cannot reproduce.

Who could benefit from this research

Good fit: Ideal candidates would be people with autism who can donate cells or tissue samples or provide clinical information for deriving patient-specific stem cells.

Not a fit: People who cannot provide biological samples or who need immediate clinical treatments are unlikely to receive direct benefit from this lab-based work.

Why it matters

Potential benefit: If successful, the work could reveal human-cell mechanisms behind autism and point to new targets for treatments.

How similar studies have performed: Prior labs have shown human interneurons can be generated from stem cells and function after transplantation into mice, but applying region-specific human interneurons to study autism genetics is a newer approach.

Where this research is happening

Newark, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Autistic Disorder
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.