Mapping genetic influences on brain function in autism and neurodevelopmental disorders

In vivo Perturb-map: scalable genetic screens with single-cell and spatial resolution in intact tissues

['FUNDING_R01'] · SCRIPPS RESEARCH INSTITUTE, THE · NIH-11011469

This study is looking at how certain genes might affect autism and developmental delays by exploring their impact on the brain, and it aims to create a new way to see how these genetic changes influence brain cells and their connections, helping us understand these conditions better.

Quick facts

Phase['FUNDING_R01']
Study typeNih_funding
SexAll
SponsorSCRIPPS RESEARCH INSTITUTE, THE (nih funded)
Locations1 site (LA JOLLA, UNITED STATES)
Trial IDNIH-11011469 on ClinicalTrials.gov

What this research studies

This research investigates how specific genetic variations contribute to autism spectrum disorder and neurodevelopmental delays by examining their effects on brain regions and neural circuits. Using advanced techniques, the team will develop a method called Perturb-map to conduct high-throughput genetic screenings in living brain tissues without the need for sectioning. This approach will allow researchers to visualize how genetic perturbations affect cell types, their locations, and connections within the brain, providing insights into the underlying mechanisms of these disorders.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with autism spectrum disorder or neurodevelopmental delays, as well as their families who may be interested in understanding the genetic aspects of these conditions.

Not a fit: Patients without a diagnosis of autism spectrum disorder or neurodevelopmental delays are unlikely to benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to a better understanding of the genetic factors involved in autism and neurodevelopmental disorders, potentially guiding new treatment strategies.

How similar studies have performed: Other research has shown success in using genetic screening techniques to understand neurodevelopmental disorders, making this approach promising yet innovative.

Where this research is happening

LA JOLLA, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.

View on NIH RePORTER →

Conditions: autism spectral disorder, autism spectrum disorder, Autistic Disorder

Last reviewed 2026-05-15 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.