Managing and supporting a research team focused on gene editing
Official title: ADMINISTRATIVE CORE
Funded at Children's Hosp of Philadelphia · NIH-10896256 · Data updated 2026-11-12
This study is all about helping a team of scientists work together better to improve gene editing techniques, making sure they stay organized and on track to develop new treatments for patients.
Quick facts
| Grant type | NIH-funded research |
|---|---|
| Study type | NIH-funded research |
| Funding institution | Children's Hosp of Philadelphia NIH-funded |
| Lab location | 1 site (Philadelphia, United States) |
| Project start | August 1, 2023 |
| Project end | July 31, 2028 |
| Funding year | 2024 |
| Award (this year) | $277,392 |
| NIH project number | 5U19NS132301-02 |
| Project ID | NIH-10896256 on NIH RePORTER |
Who could benefit from this research
✓Could help
Ideal candidates for participation or benefit from this research are individuals with genetic conditions that may be addressed through gene editing technologies.
✕Less likely to help
Patients with conditions unrelated to genetic disorders or those not eligible for gene editing therapies may not receive any benefit from this research.
What this research studies
This research involves the Administrative Core that provides essential management and logistical support for a team working on somatic cell genome editing. It aims to enhance collaboration among various research teams and ensure that project milestones are met effectively. The core will also establish a secure infrastructure for recordkeeping and facilitate communication within the research consortium, which is crucial for the success of clinical trials and innovative treatments.
Why it matters
Potential benefit: If successful, this research could streamline the development of gene editing therapies, potentially leading to new treatments for genetic disorders.
How similar studies have gone: Previous research in gene editing has shown promising results, indicating that this approach could lead to significant advancements in treatment options.
Where this research is happening
-
Children's Hosp of Philadelphia
Philadelphia, United States Active
Researchers
- Principal investigator: Musunuru, Kiran — Children's Hosp of Philadelphia
- Study coordinator: Musunuru, Kiran
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About this research
- This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
- Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
- For full project details, budget, and progress reports, visit the official NIH RePORTER page.