Lung-targeted serotonin blocker for pulmonary arterial hypertension

Systemically restricted 5-HT2B antagonists for pulmonary arterial hypertension

NIH-funded research Vanderbilt University · NIH-11261527

Developing lung-focused medicines that block a serotonin receptor to help people with pulmonary arterial hypertension.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionVanderbilt University NIH-funded
Lab location1 site (Nashville, UNITED STATES)
Project IDNIH-11261527 on NIH RePORTER

What this research studies

This project is creating new drugs that block the 5‑HT2B serotonin receptor but are designed not to enter the brain, reducing the risk of mood and sleep side effects. Researchers will choose the best lead compounds and perform safety and toxicity testing. They will test those candidates in preclinical (animal) models that mimic pulmonary arterial hypertension to see if the drugs prevent or reverse the disease. The aim is to prepare a safe lead compound for future human clinical trials.

Who could benefit from this research

Good fit: People diagnosed with pulmonary arterial hypertension who might be eligible for future clinical trials of drugs targeting the 5‑HT2B receptor.

Not a fit: Individuals with other types of pulmonary hypertension, those needing immediate therapy today, or those unable or unwilling to join clinical trials would not directly benefit from this preclinical work.

Why it matters

Potential benefit: If successful, this could produce a new PAH treatment that reduces lung blood-vessel obstruction without harmful brain-related side effects.

How similar studies have performed: Prior animal studies—including work by this team—show blocking 5‑HT2B can prevent PAH, but earlier drugs crossed into the brain and caused psychiatric side effects, making the brain‑sparing approach comparatively new.

Where this research is happening

Nashville, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.