Investigating treatments for aggressive brain cancer with specific genetic mutations

Vulnerabilities of MMR-deficient glioblastoma

NIH-funded research University of Virginia · NIH-10893006

This study is looking for new ways to treat a tough type of brain cancer called glioblastoma, especially in patients whose tumors have specific gene mutations that make them harder to treat, by testing some promising new treatments.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionUniversity of Virginia NIH-funded
Lab location1 site (Charlottesville, United States)
Project IDNIH-10893006 on NIH RePORTER

What this research studies

This research focuses on glioblastoma, a highly aggressive brain cancer that often resists standard treatments. It specifically examines glioblastomas that have mutations in DNA mismatch repair genes, making them particularly difficult to treat. The study aims to explore novel therapeutic approaches, including the use of calcium channel inhibitors and targeting TGF-β, to find effective treatments for these challenging cases. By utilizing unique tools and methodologies, the research seeks to improve outcomes for patients with MMR-deficient glioblastoma.

Who could benefit from this research

Good fit: Ideal candidates for this research are adults diagnosed with MMR-deficient glioblastoma who have not responded to standard treatments.

Not a fit: Patients with glioblastoma that does not have MMR deficiencies or those who are not adults may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatment options for patients with a form of brain cancer that currently has limited effective therapies.

How similar studies have performed: While there have been some successes in treating pediatric MMR-deficient glioblastomas with immunotherapy, adult cases have shown limited responses, making this research both novel and necessary.

Where this research is happening

Charlottesville, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.