Investigating the role of SETD1A mutations in brain disorders

Loss-of-Function Analyses of SETD1A in Human Neural Models

NIH-funded research Rutgers Biomedical and Health Sciences · NIH-11081029

This study is looking at how rare changes in a specific gene might be connected to schizophrenia and similar conditions, using special brain cells created from people’s skin cells to better understand how these changes affect brain function and could lead to new treatments.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionRutgers Biomedical and Health Sciences NIH-funded
Lab location1 site (Newark, UNITED STATES)
Project IDNIH-11081029 on NIH RePORTER

What this research studies

This research focuses on understanding how rare mutations in the SETD1A gene are linked to schizophrenia and other neurodevelopmental disorders. By using human induced pluripotent stem cells (hiPSCs) and advanced gene editing techniques, the study aims to recreate the effects of these mutations in brain cells. The researchers will analyze changes in gene expression and cellular behavior to uncover the underlying mechanisms that contribute to these mental health conditions. This approach could provide insights into the biological processes involved in schizophrenia and help identify potential therapeutic targets.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals with a diagnosis of schizophrenia or those with family histories of neurodevelopmental disorders linked to SETD1A mutations.

Not a fit: Patients without any genetic predisposition to schizophrenia or related neurodevelopmental disorders may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to new treatments or interventions for schizophrenia and related disorders.

How similar studies have performed: Previous research has shown promising results in understanding the genetic basis of schizophrenia through similar methodologies, indicating potential for success in this study.

Where this research is happening

Newark, UNITED STATES

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.