Investigating the role of leukemia stem cells in acute myeloid leukemia

Functional Interrogation of Human Acute Myeloid Leukemia Stem Cells

NIH-funded research Stanford University · NIH-11045165

This study is looking at the tiny cells that help leukemia grow, using special tools to see how changes in their genes affect the disease, with the hope of finding better treatments for people with acute myeloid leukemia.

Quick facts

Grant typeR01 grant
Study typeNIH-funded research
Funding institutionStanford University NIH-funded
Lab location1 site (Stanford, United States)
Project IDNIH-11045165 on NIH RePORTER

What this research studies

This research focuses on understanding the biology of leukemia stem cells (LSCs) in acute myeloid leukemia (AML) using advanced techniques like CRISPR/Cas9 for genome editing. By studying how specific mutations affect the behavior and frequency of these stem cells, the research aims to uncover insights into disease initiation and maintenance. The team will also create induced pluripotent stem cells (iPSCs) from AML samples to explore their potential for developing new treatments. This approach could lead to a better understanding of AML and improved therapeutic strategies for patients.

Who could benefit from this research

Good fit: Ideal candidates for this research include individuals diagnosed with acute myeloid leukemia, particularly those with specific genetic mutations.

Not a fit: Patients with other types of leukemia or those who are not diagnosed with acute myeloid leukemia may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to more effective treatments for acute myeloid leukemia by targeting the underlying stem cell mechanisms.

How similar studies have performed: Previous research has shown promise in using similar genetic engineering techniques to study cancer stem cells, indicating potential for success in this area.

Where this research is happening

Stanford, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.