Investigating new treatments for neurological diseases at the University of Rochester

University of Rochester Clinical Site within the NEXT Network of Clinical Trials

NIH-funded research University of Rochester · NIH-10878892

This study is looking for people with rare neurological conditions to join exciting clinical trials that test new gene therapies, with the hope of finding better treatments for both kids and adults.

Quick facts

Grant typeNIH-funded research
Study typeNIH-funded research
Funding institutionUniversity of Rochester NIH-funded
Lab location1 site (Rochester, United States)
Project IDNIH-10878892 on NIH RePORTER

What this research studies

This research focuses on advancing experimental therapies for neurological diseases through the University of Rochester's participation in the NeuroNEXT network. The team has a long history of leadership in this field and aims to conduct clinical trials that explore gene and gene-targeted therapies. By collaborating with a wide range of experts, the research seeks to improve trial readiness and outcomes for both children and adults affected by rare neurological conditions. Patients may have the opportunity to participate in innovative clinical trials that could lead to new treatment options.

Who could benefit from this research

Good fit: Ideal candidates include children and adults diagnosed with rare neurological diseases who are seeking new treatment options.

Not a fit: Patients with common neurological conditions or those not eligible for clinical trials may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to groundbreaking treatments for patients with neurological diseases, improving their quality of life.

How similar studies have performed: Previous research within the NeuroNEXT network has shown success in advancing treatments for neurological diseases, indicating a strong potential for this approach.

Where this research is happening

Rochester, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Last reviewed 2026-06-10 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.