Investigating new treatments for Alzheimer's disease using small molecules to target a specific enzyme.

Small Molecule Degraders of Tryptophan 2,3-Dioxygenase Enzyme (TDO) as Novel Treatments for Neurodegenerative Disease

NIH-funded research Purdue University · NIH-10991314

This study is exploring a new way to help people with Alzheimer's by targeting a specific enzyme in the brain that produces harmful substances, with the hope that a new treatment could make a positive difference for patients.

Quick facts

Grant typeFellowship grant
Study typeNIH-funded research
Funding institutionPurdue University NIH-funded
Lab location1 site (West Lafayette, United States)
Project IDNIH-10991314 on NIH RePORTER

What this research studies

This research focuses on developing innovative treatments for Alzheimer's disease by targeting the tryptophan 2,3-dioxygenase (TDO) enzyme, which is involved in the production of neurotoxic metabolites that may contribute to the disease. The approach involves using small molecules to destabilize a non-catalytic binding site on the TDO enzyme, potentially reducing the harmful effects of these metabolites in the brain. By regulating the biosynthesis of these neurotoxins, the research aims to provide a new therapeutic strategy for patients suffering from Alzheimer's disease. Patients may benefit from this research if the new treatment proves effective in clinical settings.

Who could benefit from this research

Good fit: Ideal candidates for this research are individuals diagnosed with Alzheimer's disease or those at risk of developing neurodegenerative conditions.

Not a fit: Patients with neurodegenerative diseases other than Alzheimer's or those with non-neurological conditions may not benefit from this research.

Why it matters

Potential benefit: If successful, this research could lead to a novel treatment that addresses the underlying causes of Alzheimer's disease rather than just alleviating symptoms.

How similar studies have performed: While targeting the kynurenine pathway is a relatively novel approach, preliminary studies have shown promise in similar strategies for neurodegenerative diseases.

Where this research is happening

West Lafayette, United States

Researchers

About this research

  1. This is an active NIH-funded research project — typically early-stage science, not a clinical trial accepting patient enrollment.
  2. Some NIH-funded labs run parallel clinical studies or seek volunteers for related work. To check, contact the principal investigator or institution listed above.
  3. For full project details, budget, and progress reports, visit the official NIH RePORTER page below.
Conditions Alzheimer disease dementiaAlzheimer syndromeAlzheimer's Disease
Last reviewed 2026-06-13 by the Find a Trial editorial team. Information on this page is for educational purposes and is not medical advice. Always consult qualified healthcare professionals about clinical trial participation.